Scientists from the Florida campus of The Scripps Research Institute have revealed an atomic-level view of a genetic defect that causes a form of muscular dystrophy, myotonic dystrophy type 2, and have used this information to design drug candidates with potential to counter those defects - and reverse the disease."This the first time the structure of the RNA defect that causes this disease has been determined," said TSRI Associate Professor Matthew Disney, who led the study.
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